Of all the rare diseases that have been identified globally, few have an approved treatment or therapy. Only five percent. At PPD, that number inspires us to drive research forward and to develop new rare disease therapies that change lives.
Through our Rare Disease and Pediatric Center of Excellence, wide-ranging study experience and specialized rare disease trial framework, we deliver innovative solutions to overcome the challenges associated with orphan drug development.
Watch the video animation below to learn why we are committed to advancing rare disease research.